For more information call (888) LUHS-888.
Participants with FDA-specified indications (see Appendix B for further details):
Certain lysosomal storage and peroxisomal enzyme deficiency disorders
o Hurler syndrome (MPS I)
o Krabbe Disease (Globoid Leukodystrophy)
o X-linked Adrenoleukodystrophy
Primary immunodeficiency diseases
Bone marrow failure
Signed informed consent (and signed assent, if applicable)
Pediatric and adult patients of any age
To provide access to cord blood for those recipients whose best choice for cord blood does not meet all FDA standards but does meet study standards set by the National Marrow Donor Program.
This study will assess how well and how quickly recipients blood counts return to normal after transplant.